Treatment Group Treatment Group Treatment Group Treatment Group
Treatment Response
Total (N=76) n (%) Sirolimus (N=51) n (%) Vincristine (N=25) n (%)
p-value
Any response at 3 months 53/63 (84.1%) 30/39 (76.9%) 23/24 (95.8%) 0.074
HemR at 3 months 26/27 (96.3%) 11/12 (91.7%) 15/15 (100%) 0.4
RadR at 3 months 10/21 (47.6%) 2/10 (20%) 8/11 (72.7%) 0.030
ClinR at 3 months 50/57 (87.7%) 28/34 (82.4%) 22/23 (95.7%) 0.2
Any response at 6 months 61/70 (87.1%) 38/46 (82.6%) 23/24 (95.8%) 0.2
HemR at 6 months 30/31 (96.8%) 15/16 (93.8%) 15/15 (100%) >0.9
RadR at 6 months 27/38 (71.1%) 17/25 (68%) 10/13 (76.9%) 0.7
ClinR at 6 months 59/66 (89.4%) 36/42 (85.7%) 23/24 (95.8%) 0.4